Host: Vincent Racaniello
Guest: Katherine A. High
Vincent speaks with Katherine High about her career and her work on using viral gene therapy to treat inherited disorders.
This episode is drawn from one of twenty-six video interviews with leading scientists who have made significant contributions to the field of virology, part of the new edition of the textbook Principles of Virology.
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Download TWiV 350 (28 MB .mp3, 38 min)
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Links for this episode
- Katherine A. High, MD
- Spark Therapeutics
- AAV gene therapy for congenital blindness (Sci Trans Med)
- Gene therapy for hemophilia (Hematol)
- AAV capsid decoys (Sci Trans Med)
- Video of this episode – view below or at YouTube
Send your virology questions and comments (email or mp3 file) to twiv@microbe.tv
I’m not sure if she said the name of the company she started, but I was curious. It is Spark Therapeutics, http://www.sparktx.com/
Good luck to them. It would be particularly nice for a product from UPenn to get FDA approval, given that there was some sad gene therapy history there.
Thanks for finding that, it’s clearly the right company. I’ve added it to the show notes.
Great job she and the team has done.
-BOC Sciences http://www.bocsci.com
Spark Therapeutics received the first gene therapy approval in the US. Cool to watch this now.